Treatment Options for Niemann-Pick Disease

The news concerning treatments for Niemann-Pick Disease is improving but there is still much to do before definitive therapies are available. Just a few years ago, the cause of Niemann-Pick Disease was unknown. Now the genetic sources of the disease have been identified and research is focusing on how the biochemical mechanisms work and how they can be corrected.

Potential treatments are described for informational purposes only. You should consult with your physician for medical advice about individual cases.